DDR factor depletion and focus formation analysis

Exploratory Score: 0.900 Price: $0.50 cultured cells and in vitro nucleosome system Status: proposed

What This Experiment Tests

Exploratory experiment designed to discover new patterns targeting MED1, CDK9 in cultured cells and in vitro nucleosome system. Primary outcome: Reduction in DDR foci formation

Description

This experiment examined the role of transcriptional machinery components in DNA damage response (DDR) focus formation through loss-of-function approaches. The researchers used absence or inactivation of key factors (likely RNA polymerase II, MED1, CDK9) and measured the resulting effects on DDR foci formation. The study employed both in vivo cellular systems and an in vitro reconstitution system using nucleosomes to demonstrate that these transcriptional factors are necessary for proper DDR focus assembly. This approach allowed direct testing of whether transcriptional machinery is required for the spatial organization of DNA repair factors into discrete foci.

TARGET GENE
MED1, CDK9
MODEL SYSTEM
cultured cells and in vitro nucleosome system
ESTIMATED COST
$0
TIMELINE
0 months
PATHWAY
DNA damage response pathway
SOURCE
extracted_from_pmid_31570834
PRIMARY OUTCOME
Reduction in DDR foci formation

Scoring Dimensions

Info Gain 0.00 (25%) Feasibility 0.00 (20%) Hyp Coverage 0.00 (20%) Cost Effect. 0.00 (15%) Novelty 0.00 (10%) Ethical Safety 0.00 (10%) 0.900 composite

📖 Wiki Pages

CDK9 ProteinproteinDNA Damage and Repair in NeuronscellRNA Binding Fox-1 Homolog 1 (RBFOX1)geneDNA MethylationentityDNA Damage Repair Deficiency Validation Study in PexperimentCDK9 GenegeneDNA Damage Response in Corticobasal SyndromemechanismRNA Binding Fox-1 Homolog 2 (RBFOX2)geneRNA Binding Fox-3 Homolog (NeuN) (RBFOX3)geneDNA Damage Repair Deficiency Hypothesis in ParkinshypothesisDNA Damage Repair Therapy - Biomarker GuidedideaDNA Damage Repair Investment LandscapeinvestmentRNA Therapeutics: Investment Landscape AnalysisinvestmentRNA Therapeutics for Neurodegeneration Investment investmentDNA Damage-Accumulating Neurons in Neurodegeneraticell

Protocol

DDR Factor Depletion and Focus Formation Analysis Protocol

Phase 1: siRNA Knockdown of DDR Factors in Cell Culture (Days 1-21)

Cell Line Selection: Use U2OS cells (osteosarcoma,具有良好的 DNA 损伤修复能力) for initial experiments. Maintain in DMEM + 10% FBS at 37°C, 5% CO₂. Authenticate via STR profiling, test for mycoplasma.

siRNA Transfection: Design 3 independent siRNAs per target (MED1/CD247, CDK9, and additional DDR factors: ATM, ATR, BRCA1, RNF8). Transfect U2OS at 50% confluence using RNAiMAX (Life Technologies, 30 nM siRNA, 1:1 ratio). Include non-targeting siRNA pool and untreated controls. Validate knockdown via qRT-PCR at 48h and 72h.

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Expected Outcomes

Primary Outcomes

Focus Formation Impairment: MED1 knockdown reduces IR-induced γH2AX focus formation by ≥40% (p < 0.001) and delays 53BP1 focus resolution (50% resolution time: 6h vs. 2h in controls). CDK9 knockdown produces similar but milder effects (-25% γH2AX focus number).

Promoter Occupancy: MED1 and CDK9 occupy DDR gene promoters (p21, PUMA, GADD45) at baseline and increase 3-5-fold upon DNA damage. Knockdown reduces promoter occupancy by ≥50%, confirming direct transcriptional regulation.

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Success Criteria

Primary Success Criteria

Knockdown Efficiency: Both siRNAs per target must achieve ≥65% protein reduction vs. non-targeting siRNA control (western blot densitometry), confirmed in ≥3 independent experiments.

Focus Phenotype: DDR factor knockdown must produce ≥25% reduction in IR-induced γH2AX or 53BP1 focus count at ≥1 timepoint (6h or 24h post-IR) with statistical significance (p < 0.05, n≥3 independent experiments).

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