drug

AAV

Entity Detail — Knowledge Graph Node

Understanding Entity Pages

This page aggregates everything SciDEX knows about AAV: its mechanistic relationships (Knowledge Graph edges), hypotheses targeting it, analyses mentioning it, and supporting scientific papers. The interactive graph below shows its immediate neighbors. All content is AI-synthesized from peer-reviewed literature.

18Connections
7Hypotheses
3Analyses
18Outgoing
0Incoming
6Experiments
3Debates

No summary available yet.

View on Wiki →

No AI portrait yet

💊 Drug Info
NameAAV
Key Genes/ProteinsAPOE, BDNF, Cas9, GDNF, NDNF
Related DiseasesMacaque, Rodents
Related PathwaysDescending Motor Pathways
Linked Hypotheses7 hypotheses

Wiki Pages (17)

Knowledge base pages for this entity

Canonical Page

PBKR03

entity · 3476 words

AAV Gene Therapy for Neurodevelopmental Epilepsy — Competitive Landscape & Delivery Alternatives

therapeutic · 15567 words

AAV Gene Therapy Vectors for Neurodegeneration

mechanism · 2941 words

AAV-LRRK2 IND-Enabling Study Design

experiment · 1843 words

AAV-Delivered RNA Targeting Therapy for Neurodegeneration

idea · 1497 words

AAV Gene Therapy Vectors for Neurodegenerative Diseases

therapeutic · 1465 words

Pathway Diagram

graph TD
    AAV["AAV"] -->|"associated"| Rodents["Rodents"]
    style Rodents fill:#1a2a3a,stroke:#ffd54f,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"associated"| Macaque["Macaque"]
    style Macaque fill:#1a2a3a,stroke:#ffd54f,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"targets"| NDNF["NDNF"]
    style NDNF fill:#1a2a3a,stroke:#4fc3f7,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"targets"| Brain["Brain"]
    style Brain fill:#1a2a3a,stroke:#4fc3f7,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"transports"| BDNF["BDNF"]
    style BDNF fill:#1a2a3a,stroke:#4fc3f7,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"transports"| APOE["APOE"]
    style APOE fill:#1a2a3a,stroke:#ce93d8,stroke-width:1px,color:#fff
    AAV["AAV"] -->|"transports"| GDNF["GDNF"]
    style GDNF fill:#1a2a3a,stroke:#4fc3f7,stroke-width:1px,color:#fff
    style AAV fill:#1b5e20,stroke:#4fc3f7,stroke-width:2px,color:#e0e0e0,font-weight:bold

Outgoing (18)

TargetRelationTypeStr
Rodentsexpressed_inphenotype0.90
Macaqueassociated_withphenotype0.90
Rodentsassociated_withphenotype0.90
Macaqueexpressed_inphenotype0.90
NDNFtargetsprotein0.90

Incoming (0)

SourceRelationTypeStr
No incoming edges

Targeting Hypotheses (7)

Hypotheses where this entity is a therapeutic target

HypothesisScoreDiseaseAnalysis
AAV-PHP.eB-Mediated Microglial IGFBPL1 Expression 0.720 drug delivery Can IGFBPL1 therapeutics effectively cro
AAV-Mediated APOE2/APOE3 Gene Delivery to Convert APOE Genot 0.700 neurodegeneration APOE4 targeting in neurodegeneration
TREM2 R47H Variant Correction — AAV-Mediated Rescue of Commo 0.631 Alzheimer's disease TREM2 agonism vs antagonism in DAM micro
CX3CR1-Targeted HDAC3 Knockdown in Microglia via AAV9 Delive 0.620 pharmacology How can CNS-selective HDAC/DNMT inhibito
AAV-mediated RGS6 re-expression in SNpc after pathology onse 0.530 neurodegeneration Does RGS6 upregulation or D2 autorecepto
AAV-PHP.eB-Medium OSK Expression Reverses Cortical Neuronal 0.520 neurodegeneration epigenetic reprogramming aging neurons
AAV-Mediated RGS6 Overexpression in Substantia Nigra Parvoce 0.424 neurodegeneration Does RGS6 upregulation or D2 autorecepto

Mentioning Analyses (3)

Scientific analyses that reference this entity

What delivery mechanisms can achieve therapeutically relevant CRISPR concentrati

drug delivery | 2026-04-10 | 0 hypotheses

CRISPR-based therapeutic approaches for neurodegenerative diseases

neurodegeneration | 2026-04-03 | 14 hypotheses Top: 0.803

CRISPR-based therapeutic approaches for neurodegenerative diseases

neurodegeneration | 2026-04-02 | 0 hypotheses

Experiments (6)

Experimental studies targeting or related to this entity

ExperimentTypeDiseaseScoreFeasibilityModelStatusEst. Cost
CHI3L1 variant association with AD progression in human patients exploratory Alzheimer's disease 0.850 0.00 human patients proposed N/A
AAV-LRRK2 Gene Therapy IND-Enabling Study Design clinical Parkinson's Disease 0.400 0.50 human proposed $5,460,000
AAV-LRRK2 IND-Enabling Study Design clinical Parkinson's Disease 0.400 0.50 human proposed $7,500,000
AAV Serotype Comparison for LRRK2 Knockdown in PD Gene Therapy validation Parkinson's Disease 0.400 0.50 mouse proposed $280,000
AAV Serotype Comparison for LRRK2 Knockdown in PD validation Parkinson's Disease 0.400 0.50 mouse proposed $280,000
Gene Therapy: AAV Serotype Comparison for LRRK2 Knockdown validation Parkinson's Disease 0.400 0.50 mouse proposed $280,000

Related Papers (12)

Scientific publications cited in analyses involving this entity

Title & PMIDAuthorsJournalYearCitations
The gain-of-function TREM2-T96K mutation increases risk for Alzheimer's disease [PMID:41109213] Pilat DJ, Le H, Prokopenko D, Lin CJ, Ei Neuron 2026 0
Role of TREM2 in neuroinflammation. [PMID:41213496] Abdulkhaliq AA, Alasiri G, Almoghrabi Y, Exp Neurol 2026 0
Synergistic potential of TREM2 agonists and exercise training in Alzheimer's dis [PMID:41494649] Zhang J, St Pierre Schneider B, Muguerza Am J Physiol Endocrinol Metab 2026 0
Armored macrophage-targeted CAR-T cells reset and reprogram the tumor microenvir [PMID:41576929] Mateus-Tique J, Lakshmi A, Singh B, Iyer Cancer Cell 2026 0
Peripheral cancer attenuates amyloid pathology in Alzheimer's disease via cystat [PMID:41576952] Li X, Tang X, Zeng J, Duan L, Hou Z et a Cell 2026 0
TREM2 expression level is critical for microglial state, metabolic capacity and [PMID:41580393] Feiten AF, Dahm K, Schlepckow K, van Len Nat Commun 2026 0
Large-scale single-cell analysis and in silico perturbation reveal dynamic evolu [PMID:41617928] Xia P, Shuang S, Fu D, Liu L, Yang D et NPJ Precis Oncol 2026 0
Dissecting genetic and immune drivers of heterogeneous responses to neoadjuvant [PMID:41720086] Zhao Q, Huang R, Wang C, Hu J, Nie R et Cancer Cell 2026 0
TREM2 in neurodegeneration and diseases. [PMID:41792456] ["Abdulkhaliq A", "Alasiri G", "Kim B", Molecular psychiatry 2026 0
Alzheimer's Disease as a Disorder of Neuroimmune Dysregulation. [PMID:41745721] Aranda-Abreu GE, Rojas-Durán F, Hernánde Neurology international 2026 0
Molecular mechanism of Alzheimer's disease using integrated multi-omics. [PMID:41907842] Alhusaini M, Mussa BM, Ilce BY, Alhaj H, Frontiers in aging neuroscienc 2026 0
Viral and non-viral cellular therapies for neurodegeneration. [PMID:41585268] ["Srivastav Jyotsna", "Sharma Sachin"] Frontiers in medicine 2025 0

Debates (3)

Multi-agent debates referencing this entity

All participants identified BBB penetration as a critical bottleneck, but no exi

closed · Rounds: 4 · Score: 0.50 · 2026-04-20

Evaluate the potential of CRISPR/Cas9 and related gene editing technologies for

closed · Rounds: 4 · Score: 0.95 · 2026-04-03

Evaluate the potential of CRISPR/Cas9 and related gene editing technologies for

closed · Rounds: 4 · Score: 0.90 · 2026-04-02

Related Research

Hypotheses and analyses mentioning AAV in their description or question text

AAV-PHP.eB-Medium OSK Expression Reverses Cortical Neuronal Epigenetic Age Witho

Score: 0.520 · neurodegeneration · 2026-04-22

## Mechanistic Overview AAV-PHP.eB-Medium OSK Expression Reverses Cortical Neuronal Epigenetic Age Without Altering Glia

AAV-Mediated RGS6 Overexpression in Substantia Nigra Parvocellular Neurons

Score: 0.424 · neurodegeneration · 2026-04-18

## Mechanistic Overview AAV-Mediated RGS6 Overexpression in Substantia Nigra Parvocellular Neurons starts from the claim