Doublecortin (DCX) mutations in type 1 lissencephaly

Exploratory Score: 0.800 Price: $0.50 type 1 lissencephaly human patients Status: proposed

What This Experiment Tests

Exploratory experiment designed to discover new patterns targeting doublecortin (DCX) in human patients. Primary outcome: presence of type 1 lissencephaly

Description

Analysis of human patients with mutations in the doublecortin (DCX) gene resulting in type 1 lissencephaly. The study investigated how DCX protein, which interacts with microtubules and is essential for nucleokinesis during neuronal migration, when mutated causes severe cortical malformation. This research contributed to understanding the molecular mechanisms underlying microtubule-dependent neuronal migration and the pathogenesis of lissencephaly.

TARGET GENE
doublecortin (DCX)
MODEL SYSTEM
human patients
ESTIMATED COST
$0
TIMELINE
0 months
PATHWAY
microtubule network/nucleokinesis
SOURCE
extracted_from_pmid_11429281
PRIMARY OUTCOME
presence of type 1 lissencephaly

Scoring Dimensions

Info Gain 0.00 (25%) Feasibility 0.00 (20%) Hyp Coverage 0.00 (20%) Cost Effect. 0.00 (15%) Novelty 0.00 (10%) Ethical Safety 0.00 (10%) 0.800 composite

📖 Wiki Pages

DCX GenegeneLissencephalydiseaseLissencephalydiseaseMechanismsindexNeuronal Migrationmechanism

Protocol

genetic analysis and neuropathological examination of patients with DCX mutations

Expected Outcomes

mutations in DCX would cause defective nucleokinesis leading to type 1 lissencephaly

Success Criteria

demonstration of type 1 lissencephaly phenotype in patients with DCX mutations

Related Hypotheses (0)

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