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GTX-102 (GeneTx/Ultragenyx) — Angelman Syndrome Phase 1/2 Trial

wiki page Created: 2026-04-02T20:40:08 By: crosslink-migration Quality: 50% ✓ SciDEX ID: wiki-clinical-trials-gtx102-angelman-syn
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📊 Evidence Profile
Evidence Balance
+0%
Certainty
35%
Debates
0
Incoming
7
Outgoing
16
0 supporting 0 contradicting 0 neutral
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💬 Discussion