Solve: Selective blockade of classical-pathway activation downstream of C1q will reduce synaptotoxic comple

This challenge targets the hypothesis: **Selective blockade of classical-pathway activation downstream of C1q will reduce synaptotoxic complement amplification while preserving beneficial C1q recognition functions** **Hypothesis Summary:** The most actionable synthesis is that pathogenicity may depend more on conversion of C1q binding into classical-pathway protease activity than on C1q recognition alone. In this model, inhibiting C1r/C1s should attenuate C4/C3-mediated synapse loss and neuroinflammation while preserving some homeostatic debris sensing and cargo recognition by C1q. **Falsifiable Predictions:** 1. Pharmacological modulation of C1QA will alter neurodegeneration markers in validated models by ≥20% 2. Genetic knockdown of the key target will reproduce the pathological phenotype in ≥2 independent model systems 3. Patient-derived biosamples will show the predicted molecular signature (sensitivity ≥70%, specificity ≥70%) 4. Mechanistic intervention at the proposed node will rescue neuronal viability in vitro by ≥30% **Bounty Tier:** $125,000 USD (composite score 0.750) **Challenge Type:** Open — any team may submit experimental evidence supporting or refuting this hypothesis **Success Criteria:** Peer-reviewed evidence demonstrating mechanistic validation of ≥2 of the 4 predictions, with independent replication.

$125.0K
OPEN
Confidence:
70%
Created: 2026-04-28

Scoring Dimensions

GapImportanceTherapeuticPotentialInvestmentLevelUrgencyLandscapeScore Composite score: 0.675
Gap Importance0.75
Therapeutic Potential0.00
Investment Level0.00
Urgency0.60
Landscape Score0.00
Composite Score 0.675

Linked Targets (2)

C1QA Complement C1q A Chain PDB:1PK60.55
🧬 View 3D Structure — PDB 1PK6 click to expand

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C3 Complement C3 PDB:2A730.67
🧬 View 3D Structure — PDB 2A73 click to expand

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Detected Targets:
C1QA

3D Protein Structure

View 3D structure: C1QA — PDB 1PK6

Experimental structure from RCSB PDB | Powered by Mol* | Rotate: click+drag | Zoom: scroll

Landscape analysis not yet run for this challenge. Run the landscape analyzer to get competitive intelligence.

Linked Hypotheses (1)

Selective blockade of classical-pathway activation downstream of C1q will reduce C1QA,C1QB,C1QC,C1R,C1S,C4A,C4B0.75